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Study to Assess the Long Term Safety and Efficacy of UX007 in Participants With Glucose Type 1 Deficiency Syndrome (Glut1 DS)

Glucose Transporter Type 1 Deficiency Syndrome Clinical Trial

Official title:
An Open-label Extension Study to Assess the Long-term Safety and Efficacy of UX007 in Subjects With Glucose Transporter Type 1 Deficiency Syndrome

Clinical Trial Summary

The primary objective of the study is to evaluate the long-term safety of UX007 in Glut1 DS participants.

Clinical Trial Description

The study will enroll up to 40 pediatric, adolescent and adult Glut 1 DS participants who have completed the UX007G-CL201 (NCT019933186) study and, at the discretion of the Sponsor, additional participants from other clinical studies, investigator sponsored trials (ISTs), or expanded access/compassionate use treatment. ;

Study Design

Related Conditions & MeSH terms

  • Carbohydrate Metabolism, Inborn Errors
  • Glucose Transporter Type 1 Deficiency Syndrome
  • Syndrome
Clinical Trial Details
NCT number NCT02599961
Study type Interventional
Source Ultragenyx Pharmaceutical Inc
Contact
Status Terminated
Phase Phase 2
Start date September 10, 2015
Completion date October 22, 2019
View Details
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