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NCT ID: NCT04921956 Available - Clinical trials for Congenital Haemophilia

Compassionate Use of Concizumab if You Have Haemophilia

Start date: n/a
Phase:
Study type: Expanded Access

The compassionate use programme will give participants concizumab for free, even though it is not yet approved by health authorities. This is because participants need this medicine to treat their haemophilia properly. The programme will check that participants are safe and that the medicine works for them. The programme may last for years. Participants will take one injection under their skin every day. Participants will have 4-5 visits with the study doctor for the first half year. After that they will have 1 visit every half year. At all clinic visits participants will have blood samples taken. Participants will fill in a diary between the visits. A patient is considered to have completed the programme when any of the following criteria occurred first: 1) when the patient is included in a clinical trial with concizumab or 2) up to 6 months after concizumab is commercially available in the patient's country and approved for the patient (The time span of 6 months should provide ample time for the patient to obtain concizumab commercially) or 3) the sponsor decides to discontinue concizumab clinical development for the patient's population.

NCT ID: NCT04929158 Available - Clinical trials for ST Elevation Myocardial Infarction

Comparison of Clinical Outcomes of IVUS -Guided and Angiography-guided PCI in Patients With Acute STEMI

Start date: n/a
Phase:
Study type: Expanded Access

To compare the long-term clinical outcomes of IVUS-guided vs angiography-guided PCI in patients with acute STEMI

NCT ID: NCT04959240 Available - Alpha-Mannosidosis Clinical Trials

Expanded Access to Velmanase Alfa

Start date: n/a
Phase:
Study type: Expanded Access

Individual patient expanded access requests may be considered for patients who have no other treatment options.

NCT ID: NCT04960891 Available - Uveal Melanoma Clinical Trials

A Cohort IND Expanded Access Program for Supporting Patient Access to Tebentafusp

Non Applicable
Start date: n/a
Phase:
Study type: Expanded Access

This Expanded Access Program aims to: 1. Provide access to tebentafusp for mUM patients. 2. Provide access to tebentafusp for patients, who were on the control arm of the randomized controlled Phase II trial (IMCgp100-202) and were unable to crossover during the specified window. 3. Ensure that patients, who are benefiting from tebentafusp treatment while participating in an ongoing Immunocore sponsored clinical study (e.g., IMCgp100-102 or IMCgp100-201), may continue tebentafusp treatment on this Programme once the ongoing trial has met all of its key primary and secondary objectives.

NCT ID: NCT04996134 Available - Gastroparesis Clinical Trials

Domperidone Expanded Access Treatment Program

Start date: n/a
Phase:
Study type: Expanded Access

To allow the use of domperidone by patients with gastrointestinal disorders who have failed standard therapy.

NCT ID: NCT05014607 Available - Cancer Clinical Trials

Personalized Multi-peptide Vaccination in Combination With the TLR1/2 Ligand XS15 in Cancer Patients

InHeVac01
Start date: n/a
Phase:
Study type: Expanded Access

The aim of this project is to provide personalized multi-peptide vaccination in combination with the TLR1/2 ligand XS15 to individual patients with advanced solid and hematological malignancies without any approved treatment options.

NCT ID: NCT05028166 Available - Clinical trials for Histiocytic Neoplasm

Individual Patient Compassionate Use of Mirdametinib

Start date: n/a
Phase:
Study type: Expanded Access

This program is being offered on a patient by patient basis and will require company, Institutional Review Board/Independent Ethics Committee, and applicable competent authority approval.

NCT ID: NCT05041036 Available - Desmoid Tumor Clinical Trials

Individual Patient Compassionate Use of Nirogacestat

Start date: n/a
Phase:
Study type: Expanded Access

This program is being offered on a patient by patient basis and will require company, Institutional Review Board/Independent Ethics Committee, and applicable competent authority approval.

NCT ID: NCT05047328 Available - Clinical trials for Steroid Resistant Acute Graft Versus Host Disease

Early Access Program With Inolimomab in Steroid-refractory Acute Graft Versus Host Disease

Start date: n/a
Phase:
Study type: Expanded Access

Leukotac (inolimomab) is not approved yet for marketing in any region. In the absence of medical options and based on the safety and efficacy data obtained during the clinical development program (in a phase III (INO-107) and in a Long Term Follow Up study), the French National Agency for the Medicines and Health Products Safety (ANSM) granted a Temporary Authorisation for Use (ATU) so-called cohort ATU (cATU) for LEUKOTAC® (inolimomab) and approved the temporary use protocol . This early access program has been granted to Leukotac (inolimomab) in adults and in children over 28 days of age, for treatment of acute cortico-resistant or cortico-dependent grades II-IV acute graft versus host disease (GvHD) according to the Glucksberg classification after allogeneic hematopoietic stem cell transplantation.

NCT ID: NCT05064306 Available - Clinical trials for Central Nervous System/Leptomeningeal Neoplasms

131I-omburtamab for the Treatment of Central Nervous System/Leptomeningeal Neoplasms in Children and Young Adults

Start date: n/a
Phase:
Study type: Expanded Access

The researchers are doing this study to provide access to treatment with 131I-omburtamab for children and young adults who have CNS/leptomeningeal neoplasms. 131I-omburtamab is an investigational drug; the FDA has not approved it to treat this cancer or any other disease. However, the agency has granted the drug Breakthrough Therapy Designation for the treatment of neuroblastoma with CNS metastases.