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Clinical Trial Summary

Acti-SMA is a multi-centric academic study. It aims to monitor the progress of patients with spinal muscular atrophy under treatment with Spinraza° or risdiplam. First, we want to quantify improvement of both ambulant and non-ambulant patients under treatment. A secondary objective would also be to identify suitable accelerometric measurements that are sensitive to change but also well correlated to other clinical scores.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT04888702
Study type Interventional
Source Centre Hospitalier Universitaire de Liege
Contact
Status Active, not recruiting
Phase N/A
Start date August 8, 2018
Completion date July 30, 2024

See also
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