Holter of Movement in Patients With SMA Undergoing Treatment.

Status Active, not recruiting

Clinical Trial Summary

Acti-SMA is a multi-centric academic study. It aims to monitor the progress of patients with spinal muscular atrophy under treatment with Spinraza° or risdiplam. First, we want to quantify improvement of both ambulant and non-ambulant patients under treatment. A secondary objective would also be to identify suitable accelerometric measurements that are sensitive to change but also well correlated to other clinical scores.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT04888702
Study type	Interventional
Source	Centre Hospitalier Régional de la Citadelle
Contact
Status	Active, not recruiting
Phase	N/A
Start date	August 8, 2018
Completion date	April 30, 2024

View Details

See also
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