Evaluation of Efficacy & Safety of a Single Dose of Exa-cel in

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NCT number	NCT05951205
Study type	Interventional
Source	Vertex Pharmaceuticals Incorporated
Contact	Medical Information
Phone	617-341-6777
Email	medicalinfo@vrtx.com
Status	Not yet recruiting
Phase	Phase 3
Start date	April 2024
Completion date	December 2029

Evaluation of Efficacy and Safety of a Single Dose of Exa-cel in Participants With Severe Sickle Cell Disease, βS/βC Genotype

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms