RUNX1 Familial Platelet Disorder Clinical Trial
Official title:
Protocol Title: Safety and Feasibility of Autologous CD34+ Hematopoietic Stem Cells Mobilization and Apheresis in Participants With RUNX1 Familial Platelet Disorder
To evaluate the safety and feasibility of collecting hematopoietic stem cells (HSC) in participants with RUNX1-FPD.
Primary Objective: - To evaluate the safety of harvesting HSCs in participants with RUNX1 FPD Secondary Objective - To evaluate the feasibility and other relevant information of collecting HSCs from participants with RUNX1 FPD ;