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An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett Syndrome — DAFFODIL™  

Rett Syndrome Clinical Trial

Official title:
An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett Syndrome

Clinical Trial Summary

To investigate the safety and tolerability of long-term treatment with oral trofinetide in girls with Rett syndrome

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04988867
Study type Interventional
Source ACADIA Pharmaceuticals Inc.
Contact
Status Completed
Phase Phase 2/Phase 3
Start date September 22, 2021
Completion date May 31, 2023
View Details
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