Phase 2 Study of EPI-743 for Treatment of Rett Syndrome

Status Completed

Clinical Trial Summary

Rett syndrome is a severe neurodevelopmental disorder that primarily affects female children. Rett syndrome is characterized by significant elevation in blood markers of oxidative stress. EPI-743 is a novel therapeutic with demonstrated efficacy and safety in the treatment of disorders characterized by oxidative stress. The purpose of this study is to examine the safety and efficacy of EPI-743 in a population of children with Rett syndrome.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT01822249
Study type	Interventional
Source	Edison Pharmaceuticals Inc
Contact
Status	Completed
Phase	Phase 2
Start date	January 2013
Completion date	January 2014

View Details

See also
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