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Clinical Trial Summary

The objective of this study is to obtain short- and long-term clinical safety data in pediatric and adult patients with PA and MMA treated with Carbaglu, including pregnancy and fetal outcomes. This is an observational/non-interventional study. Patients will be treated per the prescribing information and routine medical practice. Only available data will be collected as part of the study.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT05842837
Study type Observational
Source Target PharmaSolutions, Inc.
Contact
Status Enrolling by invitation
Phase
Start date September 15, 2022
Completion date June 30, 2032

See also
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