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Clinical Trial Summary

This is a non-interventional, global, multicenter, retrospective cohort study describing participant characteristics, clinical outcomes, and event rates in participants with propionic acidemia (PA).


Clinical Trial Description

This study will abstract participants data from their medical records from approximately 2015-2025. All data will be abstracted retrospectively in 6-month increments. ;


Study Design


Related Conditions & MeSH terms


NCT number NCT05769621
Study type Observational
Source ModernaTX, Inc.
Contact Moderna Clinical Trials Support Center
Phone 1-877-777-7187
Email clinicaltrials@modernatx.com
Status Recruiting
Phase
Start date June 16, 2023
Completion date March 24, 2026

See also
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