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Expanded Access for ATB200/AT2221 for the Treatment of Pompe Disease

Pompe Disease Clinical Trial

Official title:
Named Patient or Compassionate Use for Treatment Use of ATB200/AT2221 for Patients With Pompe Disease

Clinical Trial Summary

This is an expanded access program (EAP) for eligible participants designed to provide access to ATB200/AT2221.

Clinical Trial Description

This program is being offered on a patient by patient basis and will require company, IRB/IEC and single patient IND approval. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT03865836
Study type Expanded Access
Source Amicus Therapeutics
Contact For Site
Phone 609-662-2000
Email PompeSiteInfo@amicusrx.com
Status Available
Phase
View Details
See also
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