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Clinical Trial Summary

In this study the study team proposes to investigate the efficacy of albuterol on motor function of individuals with Late Onset Pompe Disease (LOPD) who are receiving enzyme replacement therapy, given albuterol was well-tolerated in patients with Late Onset Pompe Disease.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT01885936
Study type Interventional
Source Duke University
Contact
Status Completed
Phase Phase 1/Phase 2
Start date June 2013
Completion date December 16, 2016

See also
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