A Study to Evaluate the Efficacy & Safety of Alglucosidase Alfa Produced

Clinical Trial Description

n/a

Study Design

Endpoint Classification: Safety Study, Intervention Model: Single Group Assignment, Masking: Open Label, Primary Purpose: Treatment

See also
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Completed	`NCT05073783` - A Study to Assess the Safety of Myozyme® and of Aldurazyme® in Male and Female Participants of Any Age Group With Pompe Disease or With Mucopolysaccharidosis Type I (MPS I) in a Home-care Setting
Active, not recruiting	`NCT04093349` - A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)	Phase 1/Phase 2
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NCT number	NCT01526785
Study type	Interventional
Source	Sanofi
Contact
Status	Terminated
Phase	Phase 4
Start date	March 2012
Completion date	December 2014

A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe Disease

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms