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Clinical Trial Summary

This is a Phase 2 open-label, multiple dose study of BMN 701 administered by IV infusion every 2 weeks (qow) to patients with late-onset Pompe disease.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT01435772
Study type Interventional
Source BioMarin Pharmaceutical
Contact
Status Terminated
Phase Phase 2
Start date August 15, 2011
Completion date September 9, 2016

See also
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