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An Open-Label Study of Oral NNZ-2591 in Phelan-McDermid Syndrome (PMS-001) — PMS-001  

Phelan-McDermid Syndrome Clinical Trial

Official title:
An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Phelan-McDermid Syndrome (PMS-001)

Clinical Trial Summary

A study of the safety, tolerability and pharmacokinetics of NNZ-2591 and measures of efficacy in children and adolescents with Phelan-McDermid Syndrome.

Clinical Trial Description

The primary purpose of this study is to investigate the safety, tolerability and pharmacokinetics of treatment with NNZ-2591 oral solution in children and adolescents with Phelan-McDermid Syndrome. The secondary purpose is to investigate measures of efficacy. Subjects will receive treatment with NNZ-2591 oral solution (50 mg/mL) doses for a total of 13 weeks. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT05025241
Study type Interventional
Source Neuren Pharmaceuticals Limited
Contact
Status Active, not recruiting
Phase Phase 2
Start date August 8, 2022
Completion date December 31, 2023
View Details
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