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Clinical Trial Summary

This study is designed to provide continued access to BCX9930 for subjects currently receiving treatment with BCX9930 in a BioCryst-sponsored clinical study for paroxysmal nocturnal hemoglobinuria (PNH) who, in the opinion of the investigator, would benefit from continued treatment with BCX9930 and who do not have access to other treatment options.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT05741346
Study type Interventional
Source BioCryst Pharmaceuticals
Contact
Status Active, not recruiting
Phase Phase 2
Start date January 18, 2023
Completion date February 2026

See also
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