Dyskeratosis Congenita Clinical Trial
Official title:
Clinical Care Consortium of Telomere-Associated Ailments (CCCTAA) Database
Study Description: This protocol will be utilized for the creation and management of a repository of coded clinical data on patients with Telomere Biology Disorders (TBDs) submitted by researchers from CCCTAA member institutions. Objective: The primary objective of this study is to develop a shared database (repository) of coded clinical research data, managed by NCI, to facilitate collaborative research across CCCTAA member institutions.
Study Description: This protocol will be utilized for the creation and management of a repository of coded clinical data on patients with Telomere Biology Disorders (TBDs) submitted by researchers from CCCTAA member institutions. Objective: The primary objective of this study is to develop a shared database (repository) of coded clinical research data, managed by NCI, to facilitate collaborative research across CCCTAA member institutions. ;
| Status | Clinical Trial | Phase | |
|---|---|---|---|
| Completed |
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Needs Assessment for Individuals and Families Affected by Dyskeratosis Congenita (DC) and Related Telomere Biology Disorders (TBD)
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Phase 1/Phase 2 | |
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Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita
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Phase 2 | |
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N/A | |
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| Completed |
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Phase 2 | |
| Completed |
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Phase 2/Phase 3 | |
| Recruiting |
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