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Clinical Trial Details — Status: Completed

Administrative data

NCT number NCT03463265
Other study ID # GBM-007
Secondary ID
Status Completed
Phase Phase 2
First received
Last updated
Start date August 1, 2018
Est. completion date August 26, 2022

Study information

Verified date November 2023
Source Aadi Bioscience, Inc.
Contact n/a
Is FDA regulated No
Health authority
Study type Interventional

Clinical Trial Summary

Phase 2, open-label study of nab-sirolimus in patients with recurrent high grade glioma following prior therapy and patients with newly diagnosed glioblastoma. nab-Sirolimus was administered as single agent or in combination therapies.


Description:

A phase 2, open-label study of nab-sirolimus (also known as ABI-009, nab-rapamycin, albumin-bound rapamycin) in patients with recurrent high grade glioma following prior therapy and patients with newly diagnosed glioblastoma. nab-Sirolimus was administered as single agent or in combination therapies, including temozolomide, bevacizumab, lomustine, and marizomib.


Recruitment information / eligibility

Status Completed
Enrollment 62
Est. completion date August 26, 2022
Est. primary completion date August 26, 2022
Accepts healthy volunteers No
Gender All
Age group 18 Years and older
Eligibility Inclusion Criteria Specific for Arm A 1. All subjects must have histologic evidence of high grade glioma (World Health Organization [WHO] grade 3 or grade 4) and radiographic evidence of recurrence or disease progression (defined as either a greater than 25% increase in the largest bi-dimensional product of enhancement, a new enhancing lesion, or a significant increase in T2 FLAIR). Subjects must have at least 1 measurable lesion by RANO criteria (= 10 mm in 2 perpendicular diameters). 2. Patients must have previously failed a treatment regimen, including radiation and/or chemotherapy. 3. No prior treatment with mTOR inhibitors. 4. No prior treatment with temozolomide for the treatment of recurrent glioma for patients entering the ABI-009 + temozolomide cohort. 5. No prior treatment with bevacizumab or any other anti-angiogenic agents, including sorafenib, sunitinib, axitinib, pazopanib, or cilengitide for the ABI-009 + bevacizumab arm. 6. No prior treatment with lomustine for the ABI-009 + lomustine arm. 7. No prior treatment with marizomib or any other proteasome inhibitors, including bortezomib, carfilzomib, or ixazomib, for patients entering the ABI-009 + marizomib cohort. 8. At least 4 weeks from surgical resection and at least 12 weeks from the end of radiotherapy prior to enrollment in this study, unless relapse is confirmed by tumor biopsy or new lesion outside of radiation field, or if there are two MRIs confirming progressive disease that are approximately 4 weeks apart. Inclusion Criteria Specific for Arm B 1. Histologically confirmed newly diagnosed glioblastoma. 2. Patients must have had surgery and can have either non-measurable disease or a measurable post-contrast lesion after surgery detected by MRI. 3. No prior treatment with mTOR inhibitors, and no prior local or systemic therapy for GBM. Exclusion Criteria Common for Both Arms A and B A patient will not be eligible for inclusion in this study if any of the following criteria apply: 1. Co-medication or concomitant therapy that may interfere with study results, including anti-coagulants and enzyme-inducing anti-epileptic drugs (EIAEDs). 2. History of thrombotic or hemorrhagic stroke or myocardial infarction within 6 months. 3. Pregnant or breast feeding. 4. Uncontrolled intercurrent illness including, but not limited to, ongoing or active infection requiring IV antibiotics & psychiatric illness/social situations that would limit compliance with study requirements, or disorders associated with significant immunocompromised state. 5. Active gastrointestinal bleeding. 6. Uncontrolled hypertension (systolic blood pressure =160 mm Hg and/or diastolic blood pressure =90 mm Hg. 7. Patients with history of intestinal perforations, fistula, hemorrhages and/or hemoptysis =6 months prior to first study treatment. 8. Uncontrolled diabetes mellitus as defined by HbA1c >8% despite adequate therapy. 9. Patients with history of interstitial lung disease and/or pneumonitis, or pulmonary hypertension. 10. Use of strong inhibitors and inducers of CYP3A4 within the 14 days prior to receiving the first dose of ABI-009. Additionally, use of any known CYP3A4 substrates with narrow therapeutic window (such as fentanyl, alfentanil, astemizole, cisapride, dihydroergotamine, pimozide, quinidine, terfanide) within the 14 days prior to receiving the first dose of ABI-009. 11. Known other previous/current malignancy requiring treatment within = 3 years except for limited disease treated with curative intent, such as in situ prostate cancer, intracapsular renal cancer, cervical carcinoma in situ, squamous or basal cell skin carcinoma, and superficial bladder carcinoma. 12. Any comorbid condition that restricts the use of study drug and confounds the ability to interpret data from the study as judged by the Investigator or Medical Monitor. 13. Known Human Immunodeficiency Virus (HIV), or active Hepatitis B or Hepatitis C.

Study Design


Related Conditions & MeSH terms


Intervention

Drug:
nab-sirolimus
nab-sirolimus, single agent
nab-sirolimus + temozolomide
temozolomide, combination
nab-sirolimus + bevacizumab
bevacizumab, combination
nab-sirolimus + lomustine
lomustine, combination
nab-sirolimus + marizomib (MRZ)
marizomib (MRZ), combination
nab-sirolimus + temozolomide + radiotherapy
temozolomide + radiotherapy, combination

Locations

Country Name City State
United States St. Joseph Heritage Healthcare Fullerton California
United States Hoag Memorial Hospital Presbyterian Newport Beach California
United States John Wayne Cancer Institute Santa Monica California

Sponsors (1)

Lead Sponsor Collaborator
Aadi Bioscience, Inc.

Country where clinical trial is conducted

United States, 

Outcome

Type Measure Description Time frame Safety issue
Primary ORR Objective overall response rate (ORR, according to Response Assessment in Neuro-Oncology [RANO]) by investigator-assessed radiologic review and defined as the proportion of patients who achieved a confirmed partial response (PR) or confirmed complete response (CR) per RANO 2010 criteria. PR is defined as greater than or equal to 50% decrease compared with baseline in the sum of products of perpendicular diameters of all measurable enhancing lesions sustained for at least 4 weeks. Through study completion (up to 48 months)
Secondary Median PFS Progression-free Survival defined as number of months from the date of the first dose of study drug to the first observation of a disease progression or death due to any cause.
Progression is assessed according to Response Assessment in Neuro-Oncology (RANO) 2010 criteria based on MRI imaging, and includes =25% increase in the sum of the products of perpendicular diameters of enhancing lesions (compared with baseline if no decrease) on stable or increasing doses of corticosteroids.
Through study completion (up to 48 months)
Secondary PFS Rate at 6 Months and 12 Months Progression-free survival rate at 6 months and 12 months was calculated as the proportion of patients who were progression-free and alive at 6 and 12 months, respectively.
Progression is assessed according to Response Assessment in Neuro-Oncology (RANO) 2010 criteria based on MRI imaging, and includes =25% increase in the sum of the products of perpendicular diameters of enhancing lesions (compared with baseline if no decrease) on stable or increasing doses of corticosteroids.
6 and 12 months
Secondary OS Median Overall Survival Through study completion (up to 48 months)
Secondary OS at 12 Months Overall Survival rate at 12 months 12 months