Oculopharyngeal Muscular Dystrophy Clinical Trial
Official title:
Determination of Accurate Screening Tools for Dysphagia in Oculopharyngeal Muscular Dystrophy
Oculopharyngeal muscular dystrophy (OPMD) is a rare myopathic disease that results in
progressive degeneration of the oral and pharyngeal muscular, resulting in severe dysphagia
and dysarthria. OPMD is considered a rare disease; therefore, limited research is available
on the natural progression of the disease or the utility of biomarkers to identify swallowing
impairment. The aim of this study is:
1. To identify accurate, reliable and non-invasive clinical markers of swallowing
impairment
2. To determine the discriminate ability of these markers to identify impairments in
swallow safety and swallowing efficiency.
Participants will be recruited from the Neurology clinic at the University of Florida. The single evaluation will occur in the PIs research laboratory at the University of Florida, Gainesville, Florida. ;
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