Leber Hereditary Optic Neuropathy (LHON) Clinical Trial
The objective of this survey is to establish the clinical course of vision loss and recovery
in patients with a genetically confirmed diagnosis of Leber Hereditary Optic Neuropathy
(LHON).
Visual acuity changes over time from onset of symptoms and from visual acuity nadir will be
the main endpoint analysed.
The survey will collect historically documented visual acuity data for all patients at
participating sites with a genetically confirmed diagnosis of LHON. No exclusion criteria
apply. Patients are not required to attend the clinic for the survey.
Data will be collected in a completely anonymous manner. Ethical approvals and data release
agreements will be obtained as required by local regulations.
n/a
Observational Model: Case-Only, Time Perspective: Retrospective
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