An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3

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NCT number	NCT03921528
Study type	Interventional
Source	Scholar Rock, Inc.
Contact
Status	Completed
Phase	Phase 2
Start date	April 22, 2019
Completion date	February 28, 2024

An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy — TOPAZ

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms