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A Non-Interventional Post-Authorization Study of Carbaglu for the Treatment of Hyperammonemia Due to MMA and PA

Propionic Acidemia Clinical Trial

Official title:
A Non-Interventional Post-Authorization Safety Study (PASS) of Carbaglu for the Treatment of Hyperammonemia Due to Methylmalonic Acidemia (MMA) and Propionic Acidemia (PA) in Adult and Pediatric Patient Populations

Clinical Trial Summary

The objective of this study is to obtain short- and long-term clinical safety data in pediatric and adult patients with PA and MMA treated with Carbaglu, including pregnancy and fetal outcomes. This is an observational/non-interventional study. Patients will be treated per the prescribing information and routine medical practice. Only available data will be collected as part of the study.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT05842837
Study type Observational
Source Target PharmaSolutions, Inc.
Contact
Status Enrolling by invitation
Phase
Start date September 15, 2022
Completion date June 30, 2032
View Details
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