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"The MaP Study": Mapping the Patient Journey in MMA and PA

Propionic Acidemia Clinical Trial

Official title:
A Longitudinal, Exploratory, Natural History Study to Further Characterize and Describe the Signs and Symptoms of Patients With Organic Acidemias

Clinical Trial Summary

Longitudinal, exploratory, natural history study of patients with MMA due to mut deficiency and PA to characterize the changes in blood disease biomarkers over time and the frequency and severity of clinical events related to their disease.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT03484767
Study type Observational
Source ModernaTX, Inc.
Contact
Status Completed
Phase
Start date March 20, 2018
Completion date May 29, 2021
View Details
See also
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Recruiting NCT04159103 - Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia Phase 1/Phase 2