Allogeneic Stem Cell Transplantation for the Treatment of Multiple

See also
Status	Clinical Trial	Phase
Completed	`NCT00383448` - HSCT for High Risk Inherited Inborn Errors	Phase 2
Recruiting	`NCT05687474` - Baby Detect : Genomic Newborn Screening
Completed	`NCT01303146` - Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation	Phase 2
Enrolling by invitation	`NCT03655223` - Early Check: Expanded Screening in Newborns
Active, not recruiting	`NCT04628364` - The Natural History of Metachromatic Leukodystrophy Study (HOME Study)
Enrolling by invitation	`NCT05368038` - ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
Withdrawn	`NCT00639132` - The Natural History of Metachromatic Leukodystrophy
Active, not recruiting	`NCT01801709` - Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy	Phase 1/Phase 2
Completed	`NCT00683189` - Effect of Warfarin in the Treatment of Metachromatic Leukodystrophy	N/A
Recruiting	`NCT02171104` - MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis	Phase 2
Active, not recruiting	`NCT02699190` - LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies
Active, not recruiting	`NCT03392987` - A Safety and Efficacy Study of Cryopreserved OTL-200 for Treatment of Metachromatic Leukodystrophy (MLD)	Phase 2
Recruiting	`NCT02559830` - Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy	Phase 1/Phase 2
Completed	`NCT00004378` - Stem Cell Transplantation (SCT) for Genetic Diseases	N/A
Completed	`NCT00176904` - Stem Cell Transplant for Inborn Errors of Metabolism	Phase 2/Phase 3
Active, not recruiting	`NCT04283227` - OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)	Phase 3
Recruiting	`NCT03047369` - The Myelin Disorders Biorepository Project
Recruiting	`NCT04925349` - Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset Leukoencephalopathy With Axonal Spheroids and Pigmented Glia
Active, not recruiting	`NCT00005900` - Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation	N/A
Active, not recruiting	`NCT01560182` - Gene Therapy for Metachromatic Leukodystrophy (MLD)	Phase 1/Phase 2

NCT number	NCT02084121
Study type	Expanded Access
Source	Talaris Therapeutics Inc.
Contact
Status	No longer available
Phase

Allogeneic Stem Cell Transplantation for the Treatment of Multiple Sclerosis (Compassionate Use)

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms