Hypophosphatasia Clinical Trial
Official title:
A Phase 4, Randomized, Multicenter, Open-Label, 2-Dosage Regimen, Safety and Tolerability, Efficacy, Pharmacokinetic, and Pharmacodynamic Study of Asfotase Alfa in Adult Patients With Pediatric-Onset Hypophosphatasia
The study will evaluate safety, tolerability, efficacy, pharmacokinetics, and pharmacodynamics of 2 different doses (approved dose and lower dose) of asfotase alfa in adult participants with pediatric-onset hypophosphatasia (HPP).
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| Status | Clinical Trial | Phase | |
|---|---|---|---|
| Completed |
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N/A | |
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| Completed |
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Phase 3 | |
| Completed |
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Phase 2 | |
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Phase 2 | |
| Completed |
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| Completed |
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Phase 4 | |
| Completed |
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Phase 2/Phase 3 | |
| Withdrawn |
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Phase 2 | |
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