Hunter Syndrome Clinical Trial
Official title:
A Prospective, Multicenter, Single-arm, Open-label, Interventional Phase IV Study to Evaluate the Safety and Efficacy of Idursulfase (r-DNA Origin) (Elaprase™) in Indian Pediatric and Adult Population With Hunter Syndrome (Mucopolysaccharidosis II)
The main aim of this study is to learn more about the safety profile of Elaprase in Indian children and adults with hunter syndrome. Participants will receive Elaprase once per week over a 3-hour period which can be reduced to 1 hour as determined by the study doctor. Participants will need to visit the clinic weekly during the duration of the study.
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| Status | Clinical Trial | Phase | |
|---|---|---|---|
| Recruiting |
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Phase 1/Phase 2 | |
| Completed |
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||
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Phase 3 | |
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Phase 2/Phase 3 | |
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Phase 2/Phase 3 | |
| Completed |
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Phase 3 | |
| Completed |
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| Recruiting |
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Phase 2 | |
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| Completed |
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| Recruiting |
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