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Clinical Trial Summary

The aim of this prospective, observational study is to establish a dataset on the frequency of bleeding events, as well as other characteristics of bleeding events and FVIII infusions, in patients with clinically severe hemophilia A receiving prophylactic FVIII replacement therapy as standard of care. The data collected from this study may assist in providing baseline information for comparison to the Spark's investigational hemophilia A gene therapy in future Phase 3 studies.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT03876301
Study type Observational
Source Spark Therapeutics
Contact
Status Completed
Phase
Start date January 21, 2019
Completion date May 2, 2023

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