Evaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplantation in Patients With Mucopolysaccharidosis Type IH.

Hematopoietic Cell Transplantation Clinical Trial

Official title:
Evaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplantation in Patients With Mucopolysaccharidosis Type IH.

Status Recruiting

Clinical Trial Summary

This is a prospective, observational multicenter study to collect blood from patients with mucopolysaccharidosis type IH undergoing laronidase therapy and a stem cell transplant. Sixteen patients will be enrolled over a 24 month period.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT05634512
Study type	Observational
Source	Masonic Cancer Center, University of Minnesota
Contact	Kim Nelson, RN
Phone	612-273-2925
Email	knelso62@fiarview.org
Status	Recruiting
Phase
Start date	November 17, 2022
Completion date	October 1, 2025

View Details

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