Observational Study to Assess Natural History in Cockayne Syndrome Patients

Cockayne Syndrome Clinical Trial

Official title:
An Observational Study to Assess the Natural History Including Growth and Hearing in Patients With Cockayne Syndrome

Status Terminated

Clinical Trial Summary

This is an Observational Study of children under the age of 11 diagnosed with Cockayne Syndrome to assess the natural progression of Cockayne Syndrome disease, with special attention to hearing and physical changes in length or height, weight, head circumference, and arm span during standard treatment.

The primary analytical objective is to determine the rate of linear growth over a 6-month period in children < 2 years of age and over a 12-month period in children ≥ 2 years of age.

Clinical Trial Description

n/a

Study Design

Observational Model: Cohort

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT00985413
Study type	Observational
Source	DNage B.V.
Contact
Status	Terminated
Phase	N/A
Start date	September 2009
Completion date	February 2011

View Details

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