Long-term Extension of GTX-102 in Angelman Syndrome

Status Not yet recruiting

Clinical Trial Summary

The primary objective of the study is to evaluate the long-term safety profile of GTX-102 in participants with Angelman Syndrome (AS)

Clinical Trial Description

This is a Phase 3 long term extension (LTE) study to evaluate the safety and efficacy of GTX-102 in participants with AS. Participants may remain in the study until GTX-102 is approved and/or becomes available in their geographical region or the sponsor stops the study. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT06415344
Study type	Interventional
Source	Ultragenyx Pharmaceutical Inc
Contact	Patients Contact: Trial Recruitment
Phone	1-888-756-8657
Email	trialrecruitment@ultragenyx.com
Status	Not yet recruiting
Phase	Phase 3
Start date	August 2024
Completion date	February 2029

View Details

See also
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