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Clinical Trial Summary

This is a phase I/II study to evaluate the safety and efficacy of Hematopoietic Stem Cell genetherapy for the Wiskott-Aldrich Syndrome.


Clinical Trial Description

This clinical trial is an ex vivo gene therapy trial. The investigational product corresponds to autologous CD34+ cells transduced with a lentiviral vector harboring the human WASP gene. ;


Study Design


Related Conditions & MeSH terms


NCT number NCT01347346
Study type Interventional
Source Genethon
Contact
Status Completed
Phase Phase 1/Phase 2
Start date May 2011
Completion date January 9, 2017

See also
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