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Clinical Trial Summary

The trial will investigate the treatment of growth failure in children with Noonan syndrome. Abnormalities in the growth hormone (GH) – insulin-like growth factor-I (IGF-I) axis resulting in low IGF-I levels have been suggested as a possible cause of short stature seen in Noonan syndrome children. Administration of our investigational product is intended to bypass the abnormalities in the GH-IGF axis, and hopefully improve body growth.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT00351221
Study type Interventional
Source Insmed Incorporated
Contact
Status Terminated
Phase Phase 2

See also
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