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An Expanded Access Program for Risdiplam in Participants With Spinal Muscular Atrophy (SMA)

Muscular Atrophy, Spinal Clinical Trial

Official title:
An Expanded Access Program for Risdiplam in Patients With Type 1 or Type 2 Spinal Muscular Atrophy

Clinical Trial Summary

This expanded access program (EAP) will provide access to risdiplam for eligible participants with Type 1 or Type 2 spinal muscular atrophy (SMA) before it is commercially available in the United States for the indication of SMA.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04256265
Study type Expanded Access
Source Genentech, Inc.
Contact
Status Approved for marketing
Phase
View Details
See also
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