Hypophosphatasia Clinical Trial
Official title:
A Prospective Observational Sub-Study of the Global Hypophosphatasia Registry to Describe the Potential Risk of Immune-Mediated Loss of Pharmacological Effect of Asfotase Alfa in Participants With Hypophosphatasia
In this prospective observational sub-study, participants with pediatric-onset hypophosphatasia (HPP) (perinatal/infantile- or juvenile-onset) of any age will be followed for a minimum of 5 years at sites in the United States and potentially 1 or 2 other countries.
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| Status | Clinical Trial | Phase | |
|---|---|---|---|
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Phase 1/Phase 2 | |
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Phase 2 | |
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Phase 2 | |
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Phase 4 | |
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Phase 2/Phase 3 | |
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Phase 2 | |
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Phase 3 |