Angelman Syndrome Natural History Study

Status Recruiting

Clinical Trial Summary

The goal of this study is to conduct a prospective, longitudinal natural history study of children and adults with Angelman Syndrome using investigator-observed and parent-reported outcome measures to obtain data that will be useful for future clinical trials.

Clinical Trial Description

The overall goal is to increase our understanding of the long-term natural history of Angelman syndrome and obtain Angelman-specific norms for outcome measures that can be used in clinical trials, ultimately improving the care of individuals with Angelman syndrome. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT04507997
Study type	Observational
Source	Boston Children's Hospital
Contact	Wen-Hann Tan, BMBS
Phone	617-355 6394
Email	wen-hann.tan@childrens.harvard.edu
Status	Recruiting
Phase
Start date	August 1, 2018
Completion date	August 2025

View Details

See also
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