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An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome — AS-001  

Angelman Syndrome Clinical Trial

Official title:
An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome

Clinical Trial Summary

A study of the safety, tolerability and pharmacokinetics of NNZ-2591 and measures of efficacy in children and adolescents with Angelman syndrome

Clinical Trial Description

The primary purpose of this study is to investigate the safety, tolerability and pharmacokinetics of treatment with NNZ-2591 oral solution, 50mg/L, in children and adolescents with Angelman syndrome. The secondary purpose is to investigate measures of efficacy of subjects will receive treatment of 50mg/mL orally administered NNZ-2591 for a total of 13 weeks ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT05011851
Study type Interventional
Source Neuren Pharmaceuticals Limited
Contact Fernanda Cecchin
Phone +61 2 9171 3274
Email Fernanda.Cecchin@novotech-cro.com
Status Recruiting
Phase Phase 2
Start date July 12, 2022
Completion date June 30, 2024
View Details
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