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Adeno-Associated Virus (AAV) Antibody Study in Subjects OTC Deficiency, GSDIa, and Wilson Disease

Wilson Disease Clinical Trial

Official title:
Observational Clinical Study of Anti-AAV Seroprevalence in Subjects With Ornithine Transcarbamylase Deficiency, Glycogen Storage Disorder Type Ia, and Wilson Disease

Clinical Trial Summary

The objective of this observational study is to evaluate the seroprevalence of anti-AAV antibodies in subjects with Ornithine Transcarbamylase (OTC) deficiency, Glycogen Storage Disease Type Ia (GSDIa), and Wilson Disease

Clinical Trial Description

The study is primarily designed to follow a virtual model, in which Screening will take place over a telephone/video call. The study will comprise a single home health visit, either on the same day as Screening or within 30 days of enrollment. A safety follow-up may occur up to 5 days after Day 1 assessments are completed. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04909346
Study type Observational
Source Ultragenyx Pharmaceutical Inc
Contact
Status Terminated
Phase
Start date June 23, 2021
Completion date November 17, 2022
View Details
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