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Clinical Trial Summary

The primary objective of this study is to evaluate motor function following treatment with HD nusinersen in participants with spinal muscular atrophy (SMA) previously treated with risdiplam. The secondary objective of this study is to evaluate the safety and tolerability of HD nusinersen in participants with SMA previously treated with risdiplam.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT05067790
Study type Interventional
Source Biogen
Contact US Biogen Clinical Trial Center
Phone 866-633-4636
Email [email protected]
Status Not yet recruiting
Phase Phase 3
Start date November 22, 2021
Completion date June 14, 2027

See also
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