SMA Clinical Trial
Official title:
A Long-term Follow-up Study of Patients in the Clinical Trials for Spinal Muscular Atrophy Receiving AVXS-101
This is a long-term follow-up safety and efficacy study of participants in clinical trials for spinal muscular atrophy (SMA) who were treated with onasemnogene abeparvovec-xioi. Participants will roll over from their respective previous (parent) study into this long-term study for continuous monitoring of safety as well as monitoring of continued efficacy and durability of response to onasemnogene abeparvovec-xioi treatment.
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Status | Clinical Trial | Phase | |
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Not yet recruiting |
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N/A | |
Recruiting |
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Recruiting |
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Active, not recruiting |
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Phase 3 | |
Recruiting |
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Completed |
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N/A | |
Completed |
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Phase 2/Phase 3 | |
Active, not recruiting |
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Phase 3 | |
Recruiting |
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A Head-to-head Study Comparing the Functional Value of Two Models of Robotically Assisted Rehabilitation in SMA (Spinal Muscular Atrophy) Patients
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N/A | |
Completed |
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|
Phase 2 | |
Completed |
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Phase 3 | |
Completed |
NCT03921528 -
An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy
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Phase 2 | |
Active, not recruiting |
NCT05626855 -
Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab-ONYX
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Phase 3 |