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Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi

SMA Clinical Trial

Official title:
A Long-term Follow-up Study of Patients in the Clinical Trials for Spinal Muscular Atrophy Receiving AVXS-101

Clinical Trial Summary

This is a long-term follow-up safety and efficacy study of participants in clinical trials for spinal muscular atrophy (SMA) who were treated with onasemnogene abeparvovec-xioi. Participants will roll over from their respective previous (parent) study into this long-term study for continuous monitoring of safety as well as monitoring of continued efficacy and durability of response to onasemnogene abeparvovec-xioi treatment.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT04042025
Study type Interventional
Source Novartis
Contact
Status Active, not recruiting
Phase Phase 3
Start date February 10, 2020
Completion date December 31, 2035
View Details
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