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Clinical Trial Summary

In this prospective longitudinal cohort study we studied the efficacy and safety of burosumab in real-clinical practice for <13- and >13-years old children affected with X-linked hypophosphatemia.

57 children with XLH were switched from conventional treatment to burosumab. After 12 months we assessed the efficacy and safety of treatment with burosumab on the whole cohort and separately on the cohort of >13-years old adolescents.


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT04419363
Study type Interventional
Source Bicetre Hospital
Contact
Status Recruiting
Phase Phase 4
Start date March 18, 2018
Completion date September 16, 2022

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