A Retrospective Study to Characterize Participants With Propionic Acidemia

Status Recruiting

Clinical Trial Summary

This is a non-interventional, global, multicenter, retrospective cohort study describing participant characteristics, clinical outcomes, and event rates in participants with propionic acidemia (PA).

Clinical Trial Description

This study will abstract participants data from their medical records from approximately 2015-2025. All data will be abstracted retrospectively in 6-month increments. ;

Study Design

Related Conditions & MeSH terms

Propionic Acidemia

Clinical Trial Details

NCT number	NCT05769621
Study type	Observational
Source	ModernaTX, Inc.
Contact	Moderna Clinical Trials Support Center
Phone	1-877-777-7187
Email	clinicaltrials@modernatx.com
Status	Recruiting
Phase
Start date	June 16, 2023
Completion date	March 24, 2026

View Details

See also
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Terminated	`NCT04836494` - A First in Human, Dose Escalation Study to Evaluate the Safety and Tolerability of BBP-671 in Healthy Volunteers and Patients With Propionic Acidemia or Methylmalonic Acidemia	Phase 1
Completed	`NCT03484767` - "The MaP Study": Mapping the Patient Journey in MMA and PA
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Terminated	`NCT05438485` - Natural History Study of Patients With Methylmalonic Acidemia and Propionic Acidemia
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