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Clinical Trial Summary

The aim of this study is to evaluate nedosiran in participants 11 years of age and younger who have Primary Hyperoxaluria with relatively intact renal function.


Clinical Trial Description

This is an open-label, repeat-dose, Phase 2 study of nedosiran in participants 11 years of age or younger who have PH1, PH2 or PH 3 and relatively intact renal function. Following the up-to-35- day screening period, participants will return to the clinic for monthly dosing visits through Day 180. The total duration of this study is approximately 15 months from first participant, first visit, until last participant, last visit. ;


Study Design


Related Conditions & MeSH terms


NCT number NCT05001269
Study type Interventional
Source Dicerna Pharmaceuticals, Inc., a Novo Nordisk company
Contact Medical Information
Phone 617-621-8097
Email medicalinfo@dicerna.com
Status Recruiting
Phase Phase 2
Start date February 22, 2022
Completion date November 2023

See also
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