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Clinical Trial Summary

The primary objective of this study is to evaluate efficacy of danicopan as add-on treatment to ravulizumab or eculizumab as assessed by hemoglobin (Hgb) change from Baseline at Week 12 in pediatric participants with paroxysmal nocturnal hemoglobinuria (PNH) and clinically significant extravascular hemolysis (CS-EVH).


Clinical Trial Description

n/a


Study Design


Related Conditions & MeSH terms


NCT number NCT06449001
Study type Interventional
Source Alexion Pharmaceuticals, Inc.
Contact Alexion Pharmaceuticals, Inc. (Sponsor)
Phone 1-855-752-2356
Email clinicaltrials@alexion.com
Status Not yet recruiting
Phase Phase 3
Start date August 23, 2024
Completion date January 28, 2028

See also
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