US Selumetinib Registry

Status Recruiting

Clinical Trial Summary

The purpose of this study is to understand treatment patterns and assess long-term effectiveness and safety outcomes associated with selumetinib treatment as well as to explore clinical and non-clinical factors affecting those outcomes in participants with neurofibromatosis type 1 (NF1) and plexiform neurofibromas (PNs) who were aged 2 to 18 years at the time selumetinib was started in a real-world setting.

Clinical Trial Description

This is a US observational registry of pediatric NF1 PN participants treated with selumetinib. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT05683678
Study type	Observational
Source	Alexion
Contact	Alexion Pharmaceuticals, Inc.
Phone	1-855-752-2356
Email	clinicaltrials@alexion.com
Status	Recruiting
Phase
Start date	July 18, 2023
Completion date	June 21, 2028

View Details

See also
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Completed	`NCT02944032` - Efficacy of Computerized Cognitive Training and Stimulant Medication in Neurofibromatosis Type 1	N/A
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