A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria

Status Recruiting

Clinical Trial Summary

The main purpose of this study is to evaluate the long-term safety of PTC923 in participants with phenylketonuria, and to evaluate the changes from baseline in dietary phenylalanine (Phe)/protein consumption.

Clinical Trial Description

Eligible participants are: Feeder participants: those who have completed a Phase 3 PTC Therapeutics (PTC) sponsored feeder study (including Study PTC923-MD-003-PKU). Non-feeder controlled participants: those who have not completed a feeder study and have blood Phe levels <360 μmol/L at study entry. Non-feeder uncontrolled participants: those who have not completed a feeder study and have blood Phe levels ≥360 μmol/L at study entry. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details

NCT number	NCT05166161
Study type	Interventional
Source	PTC Therapeutics
Contact	Patient Advocacy
Phone	1-866-562-4620
Email	medinfo@ptcbio.com
Status	Recruiting
Phase	Phase 3
Start date	February 14, 2022
Completion date	February 7, 2025

View Details

See also
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