Sapropterin on Cognitive Abilities in Young Adults With Phenylketonuria

See also
Status	Clinical Trial	Phase
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Completed	`NCT00789568` - A Phase 1 Study to Evaluate Effects of Sapropterin Dihydrochloride on QTc Intervals in Healthy Adult Subjects	Phase 1
Terminated	`NCT01465100` - Liver Cell Transplant for Phenylketonuria	Phase 1/Phase 2
Completed	`NCT01732471` - Phase 3 Open-label Study to Evaluate the Response and Safety of Kuvan® in Subjects With Phenylketonuria	Phase 3
Completed	`NCT04879277` - Study of Low-grade Systemic Inflammation in Adult Patients With Phenylketonuria	N/A
Completed	`NCT02176603` - Observational Study of Endothelial Dysfunction in Phenylketonuria	N/A
Completed	`NCT01819727` - An Open-Label Phase 3 Study of BMN 165 for Adults With PKU Not Previously Treated w/ BMN 165	Phase 3
Completed	`NCT01869972` - Biological Variation of Phenylalanine in Patients With Hyperphenylalaninemia	N/A
Terminated	`NCT01904708` - Moderate Intensity Exercise and Phenylketonuria	N/A

NCT number	NCT01977820
Study type	Interventional
Source	BioMarin Pharmaceutical
Contact
Status	Terminated
Phase	Phase 2
Start date	February 2014
Completion date	November 2014

Sapropterin on Cognitive Abilities in Young Adults With Phenylketonuria — SIGNAL

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms