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PKUDOS: Phenylketonuria (PKU) Demographic, Outcomes, and Safety Registry — PKUDOS  

Phenylketonuria Clinical Trial

Official title:
PKUDOS: Phenylketonuria (PKU) Demographic, Outcomes, and Safety Registry

Clinical Trial Summary

The objective of this study is to evaluate the safety of long-term treatment with Kuvan.

Clinical Trial Description

The PKUDOS program is a voluntary, multicenter, strictly observational program for patients with PKU who have either received Kuvan therapy, or currently receive Kuvan, or intend to begin receiving Kuvan therapy within 90 days of entering the registry. ;

Study Design

Related Conditions & MeSH terms

Clinical Trial Details
NCT number NCT00778206
Study type Observational
Source BioMarin Pharmaceutical
Contact
Status Completed
Phase
Start date September 2008
Completion date January 29, 2021
View Details
See also
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