Observational Study to Assess the Quality of Life in Nephropathic

See also
Status	Clinical Trial	Phase
Completed	`NCT01432561` - Study in Healthy Adults to Determine the Effect That Food Has on the Absorption and Delivery of the Drug Cystagon™	N/A
Recruiting	`NCT01793168` - Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Recruiting	`NCT01327807` - Cure Cystinosis International Registry	N/A
Recruiting	`NCT03919981` - CYSTEA-BONE Clinical Study

See also

Status

Clinical Trial

Phase

Completed

NCT01432561 - Study in Healthy Adults to Determine the Effect That Food Has on the Absorption and Delivery of the Drug Cystagon™

N/A

Recruiting

NCT01793168 - Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

Recruiting

NCT01327807 - Cure Cystinosis International Registry

N/A

Recruiting

NCT03919981 - CYSTEA-BONE Clinical Study

Interventional studies are often prospective and are specifically tailored to evaluate direct impacts of treatment or preventive measures on disease.

Observational studies are often retrospective and are used to assess potential causation in exposure-outcome relationships and therefore influence preventive methods.

Expanded access is a means by which manufacturers make investigational new drugs available, under certain circumstances, to treat a patient(s) with a serious disease or condition who cannot participate in a controlled clinical trial.

Clinical trials are conducted in a series of steps, called phases - each phase is designed to answer a separate research question.

Phase 1: Researchers test a new drug or treatment in a small group of people for the first time to evaluate its safety, determine a safe dosage range, and identify side effects.
Phase 2: The drug or treatment is given to a larger group of people to see if it is effective and to further evaluate its safety.
Phase 3: The drug or treatment is given to large groups of people to confirm its effectiveness, monitor side effects, compare it to commonly used treatments, and collect information that will allow the drug or treatment to be used safely.
Phase 4: Studies are done after the drug or treatment has been marketed to gather information on the drug's effect in various populations and any side effects associated with long-term use.

NCT number	NCT04246060
Study type	Observational
Source	Chiesi SA/NV
Contact
Status	Enrolling by invitation
Phase
Start date	July 31, 2020
Completion date	July 1, 2026

Observational Study to Assess the Quality of Life in Nephropathic Cystinosis Patients — PROREAL

Clinical Trial Summary

Clinical Trial Description

Study Design

Related Conditions & MeSH terms