Biomarker Development for Muscular Dystrophies

Status Recruiting

Clinical Trial Summary

Current methods of measuring the response to new treatments for muscular dystrophies involve the examination of small pieces of muscle tissue called biopsies. The investigators are interested in finding less invasive methods that reduce the need for muscle biopsies. The purpose of this research is to learn about the possibility of detecting and measuring the activity and severity of muscular dystrophies by examining a urine sample and a blood sample, and some muscles in the arms and legs using tests called ultrasound and electrical impedance myography; both tests are painless and non-invasive. The information that is gathered from this study may help to evaluate, prevent, diagnose, treat, and improve the understanding of human muscle diseases.

Clinical Trial Description

n/a

Study Design

Related Conditions & MeSH terms

Becker Muscular Dystrophy
Duchenne Muscular Dystrophy
Facioscapulohumeral Muscular Dystrophy
Muscular Dystrophies
Muscular Dystrophy, Duchenne
Muscular Dystrophy, Facioscapulohumeral
Myotonic Dystrophy

Clinical Trial Details

NCT number	NCT05019625
Study type	Observational
Source	Massachusetts General Hospital
Contact	Tamkin Shahraki, MD
Phone	617-726-7506
Email	tshahraki@mgh.harvard.edu
Status	Recruiting
Phase
Start date	February 20, 2015
Completion date	June 2027

View Details

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